Gene Therapy for Lysosomal Storage Diseases
CHAPTER 56 Gene Therapy for Lysosomal Storage Diseases Charles H. Vite CHAPTER OUTLINE Alpha-Mannosidosis 568 Neuronal Ceroid Lipofuscinosis 570 Galactosylceramide Lipidosis 570 Gangliosidoses 570 Glycogenoses 570 Mucolipidosis 570 Mucopolysaccharidoses 570…